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Australia Approves Axatilimab for Refractory Chronic GVHD

Australia Approves Axatilimab for Refractory Chronic GVHD

Australia’s Therapeutic Goods Administration approved NIKTIMVO (axatilimab) for chronic graft-versus-host disease after failure of at least two prior systemic therapies in patients aged six and older weighing at least 40 kg. The decision followed a Priority Review pathway, expanding options for difficult-to-treat cGVHD.

Original headline

New First-in-Class Therapy for Chronic Graft-Versus-Host Disease Approved in Australia[1]